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save_the_wee_turtles6 karma

How do I build a curing chamber?

save_the_wee_turtles2 karma

Hi Melissa -

1) have you thought much about newborn screening, and if so, are you in favor of it for Hunter syndrome? 2) are you following the Sarepta story regarding their medicine for muscular dystrophy, and the pressure being applied to the FDA by patient groups after their negative report on the study results? i would be interested in your take.

thanks so much for this fascinating AMA!