heresyourfuture

Do you know what specific mutation Eli carries on his CFTR gene? Different mutations require different strategies to help CFTR do its job. There's some great research going on and therapeutics in later phase clinical trials that may be really helpful to large subsets of CF patients.

Thanks for your reply - you're probably aware of this already, but Vertex has a combination therapeutic in phase III trials right now that's showing early promise in dF508 patients. It's pretty exciting to see how the field has progressed over the last few decades. I'm hoping we see CF become long-term manageable for most cases (if not curable) in our lifetimes.