evelynsmee

Never heard of this disease, yet today I read My fight to save my daughter’s skin this morning and your AMA just now!

I found the bone marrow therapy interesting, and was particularly interested in the gene correction/replacement as there are many similarities with cystic fibrosis (ie the code to make certain proteins isn't working iirc?), which affects my family.

Anyway, I don't really have a specific question, but thank you for doing the AMA, I have been wondering about it since reading about the girl this morning, good to learn more, particularly that there were different degrees of it. Obvious really, but I hadn't thought of it.

Thanks!

I couldn't get through the questions, let alone any answers

What was it like/what happened? (that she remembers - age 4!)

Nice!

FYI, Ghana was British until independence in 1957. Old colonies tend to still use their old official language, hence the split throughout Africa of using English alongside local languages or French alongside local languages. I don't know much about what the Dutch got up to other than Afrikaans legacy.