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anxsy9 karma

Gudjon - thank for you doing this AMA, your work and for raising awareness. My mother’s side were / are carriers of Duchenne’s, with the disease afflicting two of her brothers and one of my sisters being a carrier, so this post hits home for me. I oftentimes feel like MD can be overlooked and that MDA doesn’t get the spotlight it deserves, so thank you for everything.

My question for you is how has MD treatment and therapy progressed over the last few decades? I know how things were, anecdotally from my mother, but am interested to know what technology has given.